Pegvaliase

Miglustat

Vutrisiran

Mitapivat

Chlorophyllin

Daprodustat

Dextranomer / sodium hyaluronate

Elivaldogene autotemcel

Ethanol

Etranacogene Dezaparvovec

Histamine phosphate

Aminohippurate

Trioxsalen

Benznidazole

Erythromycin / sulfisoxazole

Furazolidone

Nifurtimox

Pentamidine

Polymyxin b systemic

Metyrosine

Phentolamine

Aducanumab

Edaravone

Sodium Phenylbutyrate / Taurursodiol

Flibanserin

Indigo carmine

Maralixibat

Odevixibat

Citric acid / simethicone / sodium bicarbonate

Vosoritide